Potential Gene Therapy for Dystrophic EB, KB103, Named an Orphan Drug by FDA
A potential gene therapy for dystrophic epidermolysis bullosa (DEB), KB103 by Krystal Biotech, has been designed an Orphan Drug by the U.S. Food & Drug Administration (FDA) to help it move along in preclinical testing. KB103 is the company’s lead candidate, and is intended to treat…