• Positive Interim Results of Phase 1/2 Trial Support  FCX-007 Gene Therapy for RDEB
  • Trial Shows Abeona’s Gene Therapy EB-101 Helps Wounds Heal in RDEB Patients
  • Diacerein Ointment Granted Rare Pediatric Disease Status for EB Treatment
  • #ECRD2018 – EU Must Do More for Rare Disease Patients, Eurordis Leaders Say
  • ‘Rare Impact Awards’ Dinner Marks Orphan Drug Act and NORD at 35
  • Rare Case of Genetic and Autoimmune Subtypes of EB Described in Report
  • Krystal Biotech Doses First Patient in Phase 1/2 Trial Testing Gene Therapy Candidate KB103 for DEB
  • Collagen Vesicles Released by Bone Marrow Stem Cells May Explain Their Therapeutic Potential, Study Shows
  • Epidermolysis Bullosa Can Contribute to Esophageal Stenosis, Case Study Finds
  • #ECRD2018 – Patient Access and Collaboration Focus of Eurordis Meeting May 10-12
  • FDA Green-lights Krystal’s KB103 Gene Therapy Trial for DEB Patients
  • Human Genome Project Team at NIH Honored for Advancing Research into Genetic Diseases